Evaluating the efficacy of vatiquinone in preclinical models of Leigh syndrome and GPX4 deficiency

Simon Johnson*, Ernst-Bernhard Kayser, Michael Mulholland, Elizaveta A. Olkhova, Yihan Chen, Holly Coulson, Owen Cairns, Vivian Truong, Katerina James, Brittany M. Johnson, Allison Hanaford

*Corresponding author for this work

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
JournalOrphanet Journal of Rare Diseases
DOIs
Publication statusAccepted/In press - 28 Jan 2025

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